Manufacturing Changes and Comparability for Human Cellular and Gene Therapy Products

31 Jul.,2025

The purpose of this guidance is to provide FDA’s current thinking on 1) management and reporting of manufacturing changes for CGT products based on a lifecycle approach, and 2) comparability studies to assess the effect of manufacturing changes on product quality.

 

The management of manufacturing changes presents many challenges for human cellular therapy  or gene therapy  (CGT) products due to the complexity of these products. We, FDA, are providing you, sponsors of Investigational New Drug Applications (INDs) and applicants of Biologics License Applications (BLAs) for CGT products, with recommendations regarding product comparability and the management of manufacturing changes for investigational and licensed CGT products.

 

The purpose of this guidance is to provide FDA’s current thinking on 1) management and reporting of manufacturing changes for CGT products based on a lifecycle approach, and 2) comparability studies to assess the effect of manufacturing changes on product quality.

 

Source: FDA

Docket Number:FDA-2023-D-2436

Issued by:Center for Biologics Evaluation and Research

Download Link:https://https://www.fda.gov/media/170198/download